The First Crispr Medicine Is Now Approved in the US

The US Food and Drug Administration today approved a first-of-its kind medical treatment that uses Crispr gene editing.

Called Casgevy, the therapy is intended to treat patients with sickle cell disease, an inherited blood disorder that affects more than 100,000 people in the United States. The UK first approved the groundbreaking treatment on November 16. The therapy is made by Vertex Pharmaceuticals of Boston and Crispr Therapeutics of Switzerland.

The treatment aims to eliminate episodes of debilitating pain that are a hallmark of sickle cell disease. It involves editing patients’ cells outside the body to override the genetic defect that causes the disease. Adults and children 12 and older with frequent

→ Continue reading at Wired - Science

More from author

Related posts


Latest posts

5 Pieces of Bad Advice That Could Derail Your Business — Sidestep Disaster By Doing This Instead.

Opinions expressed by Entrepreneur contributors are their own. It is reported that nine out of ten startups fail. That's a staggering, frightening...

Fintech Sparks Personal Loan Changes for Low-Income Earners

Opinions expressed by Entrepreneur contributors are their own. This story originally appeared on Under30CEO.comThe fintech sector has transformed the personal credit business,...

Cyber Attacks Are On the Rise — Here’s How Your Business Can Continuously Prepare for Threats

Opinions expressed by Entrepreneur contributors are their own. In the ever-evolving landscape of cybersecurity threats, the traditional castle-and-moat approach is proving increasingly...